A limb-girdle muscular dystrophy 2I model of muscular dystrophy identifies corrective drug compounds for dystroglycanopathies
Publication information:
Serafini P, Feyder M, Hightower R, Garcia-Perez D, Vieira N, Lek A, Gibbs D, Moukha-Chafiq O, Augelli-Szafran C, Kawahara, Widrick J, Kunkel L, Alexander M. A limb-girdle muscular dystrophy 2I model of muscular dystrophy identifies corrective drug compounds for dystroglycanopathies.
JCI Insight. 2018;3(18):e120493.